The scientists demonstrate that it is possible to specifically deliver the treatment to the muscle stem cells, avoiding ...

The FDA has lifted its hold and has given Entrada Therapeutics permission to launch a Phase 1b clinical trial to test ...

Avidity Biosciences specializes in RNA-based therapies using Antibody-oligonucleotide conjugates to deliver drugs directly to ...

Ten of 11 children born with a rare form of congenital hearing loss experienced improvements after receiving the company’s ...

Four children born with a rare genetic form of severe blindness have all experienced significant improvements in their ...