An international research team led by Hiroki Shibuya at RIKEN Center for Biosystems Dynamics Research (BDR) in Japan has ...

Researchers have developed a DNA-based therapy that targets the PCSK9 gene to lower cholesterol naturally. Using polypurine ...

Advances in genome editing are transforming the treatment for rare genetic diseases, as seen in the case of seven-month-old ...

They observe how the mobile DNA LINE-1 copies its sequence in human cells, revealing the precise mechanism of the ORF2p gene.

Significant advancements in gene silencing and gene editing offer new hope for treating rare disorders. Techniques like RNA ...

Since 2019, MIT researchers have published a new concept called prime editing, which is more precise than regular CRISPR-Cas9 gene editing. As a result, it has fewer off-target effects and less chance ...

CRISPR-based tools can’t easily access the DNA in these organelles, but researchers are finding other ways in.

MIT scientists have found a way to make gene editing far safer and more accurate — a breakthrough that could reshape how we ...

With support from the National Institutes of Health, the COBRE Center for RNA Biology in Health and Disease will create a ...

The hereditary transthyretin amyloidosis market is experiencing significant growth driven by increasing disease awareness, ...