An international research team led by Hiroki Shibuya at RIKEN Center for Biosystems Dynamics Research (BDR) in Japan has ...

Advances in genome editing are transforming the treatment for rare genetic diseases, as seen in the case of seven-month-old ...

They observe how the mobile DNA LINE-1 copies its sequence in human cells, revealing the precise mechanism of the ORF2p gene.

Significant advancements in gene silencing and gene editing offer new hope for treating rare disorders. Techniques like RNA ...

Since 2019, MIT researchers have published a new concept called prime editing, which is more precise than regular CRISPR-Cas9 gene editing. As a result, it has fewer off-target effects and less chance ...

The hereditary transthyretin amyloidosis market is experiencing significant growth driven by increasing disease awareness, ...

P hysiology or medicine was the third prize area Alfred Nobel mentioned in his will laying out his wishes for the Nobel Prize. In 2024, the prize came with an award of 11 million Swedish krona, ...

You can always be judged by your scars. This is the idea that sums up what researchers at Spanish National Cancer Research Centre (CNIO) claim is one of the new breakthroughs in basic and biomedical ...

This is clearly good news, though there is no claim of a cure and if it can be turned into a treatment, that will surely be an expensive one. But uniQure estimates that 100,000 people in America alone ...

We’re celebrating 180 years of Scientific American. Explore our legacy of discovery and look ahead to the future. In 1957, just four years after Francis Crick and other scientists solved the riddle of ...