California’s recent decision to create a Rare Disease Advisory Council is a milestone that brings new hope to people living ...

A Kenyan toddler aged 14 months has defied the odds after surviving a rare disease that usually leads to death. Baby Arianna ...

Intercept’s US president Vivek Devaraj said the pharma company still believes in the evidence supporting the liver disease ...

to use its artificial intelligence to identify novel rare disease indications for a discontinued drug asset. Under the terms of the agreement, Sanofi will provide data related to the unnamed drug ...

Karl Fitzpatrick has described his frightening ordeal after being diagnosed with potentially life-threatening Guillain–Barré ...

but the scope of support has expanded as the "Rare Disease Control Act amendment" passed the National Assembly. Ji Young-mi, ...

Profit after tax came in ₹38.4 crore in Q2 of FY25, a recovery from a net loss of ₹11.8 crore in the first quarter of this ...

A Brisbane father has died a month after being diagnosed with an ultra-rare genetic condition that he dubbed the family “curse”. Lachlan Webb was diagnosed with the incurable genetic disease fatal ...

In a groundbreaking study, researchers at McMaster University have identified a potential treatment for Sandhoff and Tay-Sachs diseases—two rare, often fatal lysosomal storage disorders that cause ...

AstraZeneca’s growth was driven by its portfolio of products in the oncology, biopharmaceuticals and rare disease segments ...

Gurugram: Doctors at a private hospital in Haryana's Gurugram have successfully treated a 14-month-old baby from Kenya who was suffering from the extremely rare and life-threatening Pearson Syndrome.

Chhatrapati Sambhajinagar (Maharashtra) [India], November 14: Medicover Hospitals has marked a significant milestone in healthcare by successfully performing First time in Marathwada a rare and ...