Viral vectors are critical vehicles for the delivery of life-saving cell and gene therapies. Adeno-associated virus (AAV) and lentiviral vectors (LVV), two of the most widely used vector platforms, ...

This report provides an in-depth analysis of the global next-generation therapies market, highlighting key trends, growth ...

In recognition of his contributions to viral vector–based therapeutics and translation, Dr. Curiel was elected a Fellow of the National Academy of Inventors. He is also a co-founder of biotech ...

NEW YORK, Oct. 07, 2025 (GLOBE NEWSWIRE) -- Cellectis (the “Company”) (Euronext Growth: ALCLS - NASDAQ: CLLS), a clinical-stage biotechnology company using its pioneering gene-editing platform to ...

Some genetic disorders—such as cystic fibrosis, hemophilia and Tay Sachs disease—involve many mutations in a person's genome, ...

The goal of gene therapy is to permanently cure hereditary diseases. One of the most promising technologies for this is the ...

Åsa Petersén is affiliated with European Huntington Disease Network as deputy-chair of the executive committee. A company called uniQure has announced promising results from a trial of a new gene ...

A new approach to gene therapy for retinitis pigmentosa may help patients with advanced disease regain vision regardless of which genetic mutation is causing the condition. An optogenetic therapy ...

A company called uniQure has announced promising results from a trial of a new gene therapy for Huntington's disease. The news has spread quickly through families affected by this condition, who have ...

In our series “The Cost of Denial,” NBC News’ Maggie Vespa reported on brothers Noah and Hunter. Both have Duchenne Muscular Dystrophy, a rare genetic disorder that progressively attacks a person’s ...

The first participant in an investigational gene therapy trial of STXBP1 encephalopathy died, Capsida Biotherapeutics said. The death occurred days after dosing, according to information posted on the ...