Discover why Cryoport (CYRX) offers deep value for investors as the leader in temperature-controlled logistics for cell and ...

Researchers discovered that a tiny structural feature of the enzyme GPX4 helps keep neurons safe. A rare mutation removes ...

ITVISMA is a prescription gene therapy used to treat adults and children 2 years of age and older with spinal muscular atrophy (SMA). ITVISMA is given as a one-time intrathecal injection. What is the ...

A Mississippi mother and a filmmaker discuss the trials and triumphs of supporting the discovery of a gene-therapy program for a rare disease in the US.

A California toddler is the first person in the world to receive gene therapy to treat his devastating disease. ...

Genetic engineering is moving from the lab bench into clinics, farms, and even family planning decisions, promising to change ...

US FDA approves Novartis’ Itvisma, the only gene replacement therapy for children two years and older, teens, and adults with SMA: Basel Wednesday, November 26, 2025, 09:00 Hrs ...

"You could really, in a very fundamental sense, talk about redrawing the border around a brain," Hodak says, "possibly to ...

Penn Medicine shows how sustained research investment drives innovation, economic growth, and global health breakthroughs.

Hutchmed announces expanded coverage on National Reimbursement Drug List and inclusion in the first Commercial Insurance Drug List in China: Hong Kong, Shanghai Tuesday, December ...

Being selected to give an oral presentation at ASH is a tremendous honor and a major milestone,” said Sanjeev Luther, President & CEO of Ernexa Therapeutics. “It’s a recognition of the potential of ...