The first gene therapy for children with Duchenne muscular dystrophy has been approved by the U.S. Food and Drug Administration. The therapy can be used in 4- and 5-year-olds with the degenerative ...
New York, May 19, 2025 (GLOBE NEWSWIRE) -- This summer, shoppers across the U.S. have the chance to make an extraordinary difference in the lives of kids and young adults living with neuromuscular ...